A genetic neuromuscular disorder characterized by progressive muscle weakness and atrophy due to degeneration of motor neurons in the spinal cord.
| Drug Name | Mechanism | Company |
AI Value ($M)
|
Download rNPV model |
|---|---|---|---|---|
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FDA Approved Drugs
3 drugs
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Zolgensma
|
Gene therapy | Novartis |
$2377
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Evrysdi
|
Small molecule: Survival of Motor Neuron 2 Splicing Modifier | Roche |
$7368
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Spinraza
|
Oligonucleotide therapies: Survival Motor Neuron-2-directed RNA Interaction | Biogen |
$5531
|
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